Tag: Gene therapy

January 01, 2021

Development of antisense oligonucleotides for SYNGAP1 haploinsufficiency associated with autism spectrum disorder and intellectual disability

January 01, 2021

Leveraging systemic adeno-associated viral vectors to ameliorate autism-associated phenotypes in a mouse model of neurofibromatosis type 1

September 29, 2020

SFARI spring 2020 science meeting goes online By Michele Solis

Image of empty auditorium

September 01, 2020

Development of genetic therapies for STXBP1 haploinsufficiency

August 03, 2020

Antisense gene therapy for dominant haploinsufficiencies associated with autism

June 24, 2020

SFARI workshop explores challenges and opportunities of gene therapies for autism spectrum disorder By Michele Solis

Image of neurons receiving new genes